Functional delivery of oligonucleotides in vitro and in vivo
Proprietary lipids for nanoparticle formulations
In vitro functional analysis of oligonucleotides by monitoring mRNA, protein or phenotype
In vivo models to monitor cell type-specific oligonucleotide drug delivery to multiple tissues
Established delivery to hepatocytes, Stellate and Kupffer cells, endothelial cells and others, based on our proprietary platform of liponanoparticles (LNPs)
Rational oligonucleotide design tailored for specific delivery systems